::Help
Orphan drugs may be searched by product name or by name of the disease for which they are designated. Click in the appropriate box to select your option.
Product names include the trade name, compound name in English, chemical name in English, INN or code name.
Each disease is described by a name, synonyms and keywords which can be used to query the database.
You may use truncated names.
A list of all diseases or of all medicinal products matching your query will appear. Select the one of interest to you by clicking on it.
The list of Orphan Drugs in the Orphanet database includes all the medicinal products which have received an orphan designation, independently from the fact that they were further developed to become market approved drugs.
The Orphanet database also includes drugs without an orphan designation as long as they have a marketing authorisation and a specific indication for a rare disease. The lists are established using the information available at the relevant governmental agencies, and information provided by sponsors of medicinal products with an orphan designation when the product is not yet marketed.
::Warning
Orphanet acknowledges the contribution of the European Medicines Agency (EMEA) in the creation of the database on orphan medicinal products in Europe. This project was initiated by the Committee for Orphan Medicinal Products - Working Group with Interested Parties (COMP-WGIP) at the EMEA. Several members of the COMP-WGIP have individually contributed to the development of the database, which was welcomed by the COMP-WGIP as a significant tool for all interested parties.
The database has been developed entirely and autonomously by ORPHANET - INSERM SC11 France, using public and private funding and on publicly available data; as such, the EMEA or the COMP-WGIP are not responsible for the content and management of the database.
The Orphanet database of orphan drugs was developped with co-funding from the following institutions and companies:
