Orphan Designations by geographical area
- C1-esterase inhibitor
- Caffeine citrate
- Canakinumab
- Carbetocin
- Carboxypeptidase G2
- Cardiotrophin-1
- Carfilzomib
- Carglumic acid
- Carmustine
- Carmustine (solution for intratumoral injection)
- Catridecagog
- Catumaxomab
- Celecoxib
- Cenersen
- Cetuximab
- Chimeric antibody to mesothelin
- Chimeric-anti-interleukin-6 monoclonal antibody
- Chimeric IgG monoclonal antibody cG250
- Chimeric locked nucleic acid-deoxynucleoside phosphorothioate-linked oligonucleotide directed against microRNA-451
- Chimeric monoclonal antibody against claudin-18 splice variant 2
- Chimeric monoclonal antibody against claudin 6
- Chimeric monoclonal antibody against GD2
- Chimeric monoclonal antibody against kappa myeloma antigen
- Chimeric monoclonal antibody to shiga-toxin 1 and 2
- Chlormethine
- Cholest-4-en-3-one, oxime
- Cholic acid
- Choline tetrathiomolybdate
- Ciclosporin
- Ciclosporin (eye drops, solution)
- Ciclosporin (inhalation use)
- Cilengitide
- Cinacalcet
- Ciprofloxacin (inhalation use)
- Ciprofloxacin (lisosomal)
- Cisplatin (liposomal)
- Cladribine
- Cladribine (subcutaneous use)
- Clofarabine
- Clofazimine
- Clonidine hydrochloride
- Colchicine
- Concentrate of proteolytic enzymes enriched in bromelain
- Covalently closed DNA plasmids coding for cytomegalovirus phosphoprotein 65 and glycoprotein B genes
- Crisantaspase
- Cyclic pyranopterin monophosphate
- Cyclo-Cys-Gly-Gln-Arg-Glu-Thr-Pro-Glu-Gly-Ala-Glu-Ala-Lys-Pro-Trp-Tyr-Cys
- Cyclo(-gamma-aminobutyryl-L-phenylalanyl-L-tryptophanyl-D-tryptophanyl-L-lysyl-L-threonyl-L phenylalanyl-N-3-carboxypropyl)-glycine amide, acetate salt
- Cyclo[L-alanyl-L-seryl-L-isoleucyl-L-prolyl-L-prolyl-L-glutaminyl-L-lysyl-L-tyrosyl-D-prolyl-L-prolyl-(2S)-2-aminodecanoyl-L-alpha-glutamyl-L-threonyl] acetate salt
- Cyclopropane-1,1-dicarboxylic acid [4-(6,7-dimethoxy-quinolin-4-yloxy)-phenyl]-amide (4-fluoro-phenyl)-amide, (L)-malate salt
- Cysteamine
- Cysteamine bitartrate (gastroresistant capsule)
- Cysteamine hydrochloride
- Cytochrome P450 isoform 2B1 gene transfected human embryonic kidney 293 cells encapsulated in polymeric cellulose sulphate
