Orphan Designations by geographical area
- (E)-2,4,6-trimethoxystyryl-3-carboxymethylamino-4-methoxybenzyl-sulfone sodium salt
- Ecallantide
- E. Coli heat-shock protein 70 with bovine retinal S-antigen
- Ecopipam
- Ecteinascidin 743
- Eculizumab
- Eflornithine
- Eflornithine hydrochloride
- Eflornithine in combination with sulindac
- Eicosapentaenoic acid
- Elafin
- Elotuzumab
- Eltrombopag olamine
- Encapsulated human retinal pigment epithelial cell line transfected with plasmid vector expressing human ciliary neurotropic factor
- Engineered protein inhibitor of human neutrophil elastase
- Entinostat
- Enzastaurin hydrochloride
- Epoprostenol
- Epratuzumab
- Eptacog alfa (activated)
- Erdosteine
- Erlotinib hydrochloride
- Estradiol Hemihydrate and Progesterone
- Etanercept
- Ethanol (96 per cent) (gel for injection)
- Ethyl Eicosopentaenoate
- Etilefrine
- Everolimus
- Exon 44 specific phosphorothioate oligonucleotide
- Exon 45 specific phosphorothioate oligonucleotide
- Exon 51 specific phosphorothioate oligonucleotide
- Exon 52 specific phosphorothioate oligonucleotide
- Exon 53 specific phosphorothioate oligonucleotide
- Exon 55 specific phosphorothioate oligonucleotide
- Expanded Allogeneic Human Dermal Fibroblasts In Hypothermosol(R)-Frs
- Expanded human allogeneic mesenchymal adult stem cells extracted from adipose tissue
- Extract of Sorghum bicolour leaf, Pterocarpus osun stem, Piper guineense seed and Caryophylli flower
- Ex-vivo cultured adult human mesenchymal stem cells
- Ex vivo expanded autologous human corneal epithelium containing stem cells
