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Orphan Designations by geographical area
- R-1-[2,3-dihydro-2-oxo-1-pivaloylmethyl-5-(2-pyridyl)-1H-1,4-benzodiazepin-3-yl]-3-(3-methylaminophenyl)urea
- (R)-2-Methyl-6-nitro-2-{4-[4-(4-trifluoromethoxyphenoxy)piperidin-1-yl]phenoxymethyl}-2,3-dihydroimidazo[2,1-b]oxazole
- (R)-3-(4-(7H-pyrrolo[2,3-d]pyrimidin-4-yl)-1H-pyrazol-1-yl)-3-cyclopentylpropanenitrile phosphate
- Rabies immune globulin (human)
- Raloxifene hydrochloride
- Ramiprilat
- Ramoplanin
- Ramucirumab
- Ranpirnase
- Rapamycin (mTOR) inhibitor
- R-baclofen
- Recombinant adeno-associated viral vector containing human acid alfa-glucosidase-gene
- Recombinant adeno-associated viral vector containing human alpha-1 antitrypsin gene
- Recombinant adeno-associated viral vector containing the human CNGB3 gene
- Recombinant adeno-associated viral vector containing the human retinoschisin gene
- Recombinant antibody construct against human CD30 and CD16A
- Recombinant antibody derivative against human CD19 and CD3
- Recombinant anti-CD3-bi-single-chain-Fv-diphtheria toxin fusion protein
- Recombinant anti-CD40 monoclonal antibody
- Recombinant chimeric monoclonal antibody against CD20
- Recombinant derivative of C3 transferase
- Recombinant dog gastric lipase
- Recombinant fusion protein consisting of human coagulation factor IX attached to the Fc domain of human IgG1
- Recombinant fusion protein consisting of human coagulation factor VIII attached to the Fc domain of human IgG1
- Recombinant fusion protein consisting of the extracellular portion of CD95 fused to the Fc part of a human IgG1 molecule
- Recombinant fusion protein consisting of the extracellular portion of human activin receptor IIB linked to the human IgG1 Fc domain
- Recombinant fusion protein linking human coagulation factor IX with human albumin
- Recombinant fusion protein linking human coagulation factor VIIa with human albumin
- Recombinant fusion protein of circulary-permuted IL-4 and pseudomonas exotoxin A, [IL-4(38-37)-PE38KDEL]
- Recombinant glycoprotein gp350 of Epstein-Barr virus
- Recombinant histidine-tagged idiotype immunoglobulin Fab fragment of clonal B-cell receptors
- Recombinant homodimer of the human annexin V
- Recombinant human acid alpha-glucosidase
- Recombinant human acid sphingomyelinase
- Recombinant human ADAMTS-13
- Recombinant human alpha-1-antitrypsin (respiratory use)
- Recombinant Human Alpha-Fetoprotein (Rhafp)
- Recombinant human alpha-mannosidase
- Recombinant human anti-interferon gamma monoclonal antibody
- Recombinant human arylsulfatase A
- Recombinant human beta-glucuronidase
- Recombinant human bile salt-stimulated lipase
- Recombinant human C1-inhibitor
- Recombinant human CXCL8 mutant
- Recombinant human dyskerin
- Recombinant human elafin
- Recombinant human galactocerebrosidase
- Recombinant human heat shock protein 70
- Recombinant human heparan-N-sulfatase
- Recombinant human hepatitis C monoclonal antibody against C4 region of E1
- Recombinant human hepatocarcinoma-intestine-pancreas / pancreatic associated protein
- Recombinant human histone H1.3 and recombinant human N-bis-met-histone H1.3
- Recombinant human interleukin-21
- Recombinant human interleukin-7
- Recombinant humanised anti-human interleukin-1 beta monoclonal antibody
- Recombinant humanised monoclonal antibody to human Nogo-A protein of the IgG1/kappa class
- Recombinant human lysosomal acid lipase
- Recombinant human methionine proinsulin
- Recombinant human minibody against complement component C5
- Recombinant human minibody against complement component C5 fused with RGD-motif
- Recombinant human monoclonal antibody against activin receptor type IIB
- Recombinant human monoclonal antibody against transforming growth factor beta-1, 2 and 3
- Recombinant human monoclonal antibody of the IgG1 kappa class against prostate stem cell antigen
- Recombinant human monoclonal antibody to human Interleukin (IL)-17A of the IgG1/k class
- Recombinant human monoclonal antibody to human Nogo-A protein of the IgG4/kappa class
- Recombinant human N-acetylgalactosamine-6-sulfatase
- Recombinant human pentraxin-2
- Recombinant Human Porphobilinogen Deaminase
- Recombinant human proinsulin
- Recombinant human rod-derived cone viability factor
- Recombinant human serum amyloid P
- Recombinant human soluble Fc-gamma receptor II b
- Recombinant human tissue non-specific alkaline phosphatase - Fc - deca-aspartate fusion protein
- Recombinant human tripeptidyl-peptidase 1
- Recombinant human vascular endothelial growth factor
- Recombinant human von Willebrand factor
- Recombinant inhibitor of human plasma kallikrein
- Recombinant kallikrein inhibitor
- Recombinant megakaryopoeisis-stimulating protein
- Recombinant microbial lipase
- Recombinant modified human growth hormone
- Recombinant modified vaccinia Ankara expressing human 5T4
- Recombinant modified vaccinia virus Ankara expressing tuberculosis antigen 85A
- Recombinant porcine factor VIII (B domain deleted)
- Recombinant protein consisting of modified human growth hormone releasing hormone and the translocation and endopeptidase domains of botulinum toxin serotype D
- Recombinant P-selectin glycoprotein immunoglobulin
- Recombinant thymidine phosphorylase encapsulated in autologous erythrocytes
- Regorafenib
- Reparixin
- Repertaxin L-lysine salt
- Resminostat
- Retroviral gamma-c cDNA containing vector
- Ribonucleotide reductase R2 specific phosphorothioate oligonucleotide
- Rifampicin
- Rifampicin, isoniazid, pyrazinamide
- Rifapentine
- Rilonacept
- Riluzole
- Rituximab
- RNA, [P-deoxy-P-(dimethylamino)] (2',3'-dideoxy-2',3'-imino-2',3'-seco) (2'a-->5') (C-m5U-C-C-A-A-C-A-m5U-C-A-A-G-G-A-A-G-A-m5U-G-G-C-A-m5U-m5U-m5U-C-m5U-A-G), P-[4[[2-[2-(2-hydroxyethoxy)ethoxy]ethoxy]carbonyl]-1-piperazinyl] N,N-dimethylaminophosphonamidate
- RNA, [P-deoxy-P-(dimethylamino)] (2',3'-dideoxy-2',3'-imino-2',3'-seco) (2'a-->5') (C-m5U-m5U-A-C-A-G-G-C-m5U-C-C-A-A-m5U-A-G-m5U-G-G-m5U-C-A-G-m5U), 5' [P-[4-[[2-[2-(2-hydroxyethoxy)ethoxy]ethoxy]carbonyl]-1-piperazinyl]-N,N-dimethylaminophosphonamidate], 3'-[2'a-[------], octahydrochloride
- Romidepsin
- R-salbutamol sulphate
- Rubitecan
- Rufinamide
