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Designaciones huérfanas por área geográfica
- Ma09-Hrpe Cells
- Macitentan
- Maleato de hidrógeno de lisurida
- Maleato de nimorazol
- Mammalian target of rapamcyin (mTOR) inhibitor
- (manganese, dichloro [(4aR, 13aR, 17aR, 21aR)-1, 2, 3, 4, ...tetraazacycloheptadecine-kN5, kN13, kN18, kN21, kN22]-)
- Mannitolum
- Maribavir
- Mavoglurant
- Maytansinoid-conjugated human monoclonal antibody against mesothelin
- Mecasermin
- Mecasermin rinfabate
- Mefloquina clorhidrato de
- Melarsoprol
- Melatonina
- Melfalam
- Meloxicam
- Mepolizumab
- Mercaptopurina (suspensión oral)
- Mercaptopurine (oral liquid)
- Mesilato de masitinib
- Mesilato de nafamostat
- Metastable technetium 99 [99mTc] Demogastrin 2
- Methotrexate (oral liquid)
- Methotrexato
- Methoxsalen
- Methyl 4,6-diamino-2-[1-(2-fluorobenzyl)-1H-pyrazolo[3,4-b]pyridine-3-yl]-5-pyrimidinyl(methyl)carbamate
- Methyl O-4-O-[2-[2-[2-[2-[[N-[(1R)-1-[[4-(aminoiminomethyl)phenyl]methyl]-[-----]-D-glucopyranoside 2,6-bis(hydrogen sulfate) octasodium salt
- Metiltionina
- Metreleptin
- Metronidazole
- Mibefradil
- Microvesícula multilamelar que comtiene fosfatidilcolina, esfingomielina, fosfatidiletanolamina, fosfatidilserina, fosfatidilinositol y colesterol
- Midodrine hydrochloride
- Midostaurina
- Mifamurtide
- Mifepristona
- Migalastat hydrochloride
- Milatuzumab
- Milciclib maleate
- Miltefosine
- Minianticuerpo recombinante humano contra el factor C5 del complemento
- Minianticuerpo recombinante humano fusionado con el motivo RGD contra el factor C5 del complemento
- Mitotane
- Mitoxantrone
- Mixture of two allogeneic human pancreatic cancer cell lines stably transduced with a retroviral vector encoding the murine alpha-(1,3)-galactosyltransferase gene
- Modafinil
- Modified recombinant human C-type natriuretic peptide
- Mogamulizumab
- Monarsen
- Monoclorhidrato de 8-[4-(1-aminociclobutil)fenil]-9-fenil-1,2,4-triazolo[3,4-f][1,6]naftiridin-3(2H)- ona
- Monohidrato de sal de (3S)-3-{4-[7-(aminocarbonil)-2H-indazol-2-il] fenil} piperidina tosilato
- Moroctocog alpha
- Mycobacterium vaccae termoinactivado (de célula entera)
- Mycophenolate mofetil