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Désignations orphelines par zone géographique
- 11-(2-pyrrolidine-1-yl-éthoxy)-14,19-dioxa-5,7,26-triaza-tétracyclo[19.3.1.1(2,6).1(8,12)] heptacosa-1(25),2(26),3,5,8,10,12(27),16,21,23-décaène
- 1,2:5,6-Dianhydrogalactitol
- 1-[2-(Benzo[1,2,5]thiadiazol-5-ylamino)-6-(2,6-dichloro-phényl)-pyrido[2,3-d]pyrimidin-7-yl]-3-tert-butyl-urée
- 1,2-bis(methylsulphonyl)-1-(2-chloroethyl)-2-[(methylamino)carbonyl]hydrazine
- 1-[(2-Chloro-4-methoxyphenoxy)methyl]-4-[(2,6-dichlorophenoxy)methyl]benzene
- 1-{3-[3-(4-chlorophenyl)propoxy]propyl}piperidine, hydrochloride
- 1-[(3R)-3-[4-amino-3-(4-phénoxyphényl)-1H-pyrazolo[3,4d]pyrimidin-1-yl]-1-pipéridinyl]-2-propène-1-one
- 1-(4-{4-amino-7-[1-(2-hydroxyéthyl)-1H- pyrazol-4-yl]thieno[3,2-c]pyridine-3-yl}phényl)-3-(3-fluorophényl)urée
- 1,5-(Butylimino)-1,5-dideoxy, D-glucitol
- 17-allylamino-17-demethoxygeldanamycin
- (-)-17-(cyclopropylmethyl)-3,14 ß-dihydroxy-4,5 a-epoxy-6ß-[N-methyl-trans-3-(3-furyl) acrylamido] morphinan hydrochloride
- 17-(Dimethylaminoethylamino)-17-demethoxygeldanamycin (after administration of adeno-associated viral vector encoding an inducible short hairpin RNA targeting claudin-5)
- 1-cyclopropyl-3-[3-(5-morpholin-4-ylméthyl-1H-benzoimidazol-2-yl)-1H-pyrazol-4-yl]-urée
- 1-deoxynojirimycin hydrochloride
- 1H-Benzimidazole-7-carboxamide, 2-[(2R)-2-methyl-2-pyrrolidinyl]
- (1-méthyl-2-nitro-1H-imidazole-5-yl)méthyl N,N'-bis(2-bromoéthyl) diamidophosphate
- (1R,2R)-octanoic acid[2-(2',3'-dihydro-benzo[1,4] dioxin-6'-yl).....-tartaric acid salt
- (1R,2S) 6-bromo-alpha-[2-(dimethylamino)ethyl]-2-methoxy-alpha-(1-naphthyl)-beta-phenyl-3-quinolineethanol
- 20-pentaérythritol poly (oxy-1,2-ethandiyl)-carboxyméthyl-glycinate-7-ethyl-10-hydroxycamptothécine 10-[1,4'-bipipéridine]-1'-carboxylate
- 2,2'-{2-[(1R)-1-({[(2,5-dichlorobenzoyl)amino]acétyl}amino)-3-méthylbutyl]-5-oxo-1,3,2-dioxaborolane-4,4-diyl}diacétique
- 2-(2-chlorophényl)-4-[3-(diméthylamino)phényl]-5-méthyl-1H-pyrazolo[4,3-c]pyridine-3,6(2H, 5H)-dione
- 2-[[3-({4-[(5-{2-[(3-Fluorophenyl)amino]-2-oxoethyl}- 1H-pyrazol-3-yl)amino]- quinazolin-7-yl}oxy)propyl](ethyl)amino]ethyl dihydrogen phosphate trihydrate
- 2,3,4,5 tétrahydro-2,8-diméthyl-5-[2-(6-méthyl-3-pyridyl)éthyl]-1H-pyrido[4,3-b]indole dichlorhydrate
- 2',3',5'-tri-O-acétyluridine
- 2-{4-[(5,6-diphenylpyrazin-2-yl)(isopropyl)amino]butoxy}-N-(methylsulfonyl)acetamide
- 2-[4-Methoxy-3-(2-m-tolyl-ethoxy)-benzoylamino]-indan-2-carboxylic acid
- 2-allyl-1-[6-(1-hydroxy-1-méthyléthyl)pyridine-2-yl]-6-{[4-(4-méthylpiperazine-1-yl)phényl]amino}-1,2-dihydro-3H-pyrazolo [3,4-d]pyrimidine-3-one
- [2-Cyano-3-cyclopropyl-3-hydroxy-N-(3-methyl-4-trifluoromethylphenyl)prop-2-enamide]
- 2-Iminobiotine
- 2-Methoxy-5-[(1Z)-2-(3,4,5-trimethoxyphenyl)ethenyl]-phenol
- 2-méthoxyméthyle-2-hydroxyméthyle-1-azabicyclo[2,2,2]octane-3-one
- (2R)-3-(2-hydroxymethylindanyl-4-oxy)-phenyl-4,4,4-trifluorobutane-1-sulfonate
- (2S)-2-{[(2R)-2-[({[3,3-dibutyl-7-(methylthio)-1,1-dioxido-5-phenyl-2,3,4,5-tetrahydro-1,2,5-benzothiadiazepin-8-yl]oxy}acetyl)amino]-2-(4-hydroxyphenyl)acetyl]amino}butanoic acid
- 2S 4R ketoconazole
- 3,4-diaminopyridine phosphate
- (3-[5-(2-fluoro-phenyl)-[1,2,4]oxadiazole-3-yl]-benzoic acid
- 3-(6-(1-(2,2-difluorobenzo [d] [1,3]dioxol-5-yl)cyclopropanecarboxamido)-3-méthylpyridine-2-yl) acide benzoïque
- 3-methoxy-pregnelonone
- (3S)-3-{4-[7-(aminocarbonyl)-2H-indazol-2-yl] phényl} piperidine sel de tosylate monohydrate
- 4-[123I] iodo-L-phenylalanine
- 4-[131I]iodo-L-phenylalanine
- 4-[2-(6-methylpyridin-2-yl)-5,6-dihydro-4H-pyrrolo[1,2-b]pyrazol-3-yl]-quinoline-6-carboxamide monohydrate
- 4-[3-(methylsulfonyl)phenyl]-1-propylpiperidine x HC1
- 4-(4-{[2-(4-chlorophenyl)-4,4-dimethylcyclohex-1-en-1-yl]methyl}piperazin-1-yl)-N-({3-nitro-4-[(tetrahydro-2H-pyran-4-ylmethyl)amino]phenyl}sulfonyl)-2-(1H-pyrrolo[2,3-b]pyridin-5-yloxy)benzamide
- 4,6,8-trihydroxy-10-(3,7,11-triméthyldodéca-2,6,10-triènyl)-5,10-dihydrodibenzo[b,e][1,4]diazépine-11-one
- 4,7,10,13,16,19-Docosahexaenoic acid
- 4-[[9-[(3S)-tetrahydro-3-furanyl]-8-[(2,4,6-trifluorophenyl)amino]-9H-purine-2-yl]amino]-trans-cyclohexanol
- 4-amino-5-oxo-4 (pyridinium-1-ylmethyl) proline
- 4-amino-(6R,S)-5,6,7,8-tetrahydro-L-biopterin dihydrochloride
- 4-Amino-...-D-arabinofuranosyl]-...pyrimidinone
- 4-aminopyridine
- 4-benzyl-2-naphtalène-1-yl-1,2,4-thiadiazolidine-3,5-dione
- 4-ethoxy-2-(piperazin-1-yl)-7-(pyridin-4-yl)-5H-pyrimido[5,4-b]indol
- 4-imino-1, 3-diazobicyclo-[3.1.0]-hexan-2-one
- 5-[1-(2,6-dichlorobenzyl)pipéridine-4-ylméthoxy]quinazoline-2,4-diamine dihydrochloride
- 5-(2,6-Difluoro-phenoxy)-3(R,S)-{2(S)-[2(S)-(3-methoxycarbonyl-2(S)-{3-methyl-2(S)-[(quinoline-2-carbonyl)-amino]-butyrylamino}-propionylamino)-3-methyl-butyrylamino]-propionylamino}-4-oxo-pentanoic acid methyl ester
- 5-aminolevulinic acid hydrochloride
- 5'-CTG CCA CGT TCT CCT GC-(2' methoxy)A-(2' methoxy)C-(2' methoxy)C-3'
- 5-(ethylsulfonyl)-2-(naphthalen-2-yl)benzo[d]oxazole
- 5-methyl-pyridine-2-sulfonic acid {6-(2-hydroxy-ethoxy)-5-(2-methoxy-phenoxy)-2-...-amide sodium salt
- 5'-O-(trans-9''-octadécenoyl)-1-beta-D-2'-deoxy-2',2'-difluorocytidine
- 5'-O-(trans-9"-octadecenoyl)-1-ß-D-arabinofuranosyl cytosine
- 5(S)-(2'-hydroxy ethoxy)-20(S)-camptothecin
- 6-chloro-2,3,4,9-tétrahydro-1H-carbazole-1-carboxamide
- 6-éthynyl-1-(pentan-3-yl)-1H-imidazo[4,5-b]pyrazine-2(3H)-one
- (6R)-4, 5, 6, 7-tetrahydro-N6-propyl-2, 6-benzothiazolediamine dihydrochloride monohydrate
- 6-thioguanine (liquide oral)
- 7-beta-hydroxy cholesteryl-3-beta-oleate
- 9 cis rétinyl acetate