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Designazioni Orfane per area geografica
- 11-(2-pirrolidin-1-yl-etossi)-14,19-diossa-5,7,26-triaza-tetraciclo[19.3.1.1(2,6).1(8,12)] eptacosa-1(25),2(26),3,5,8,10,12(27),16,21,23-decene
- 1,2:5,6-Dianhydrogalactitol
- 1-[2-(Benzo[1,2,5]tiadiazol-5-ilamino)-6-(2,6-dicloro-fenil)-pirido[2,3-d]pirimidin-7-il]-3-tert-butil-urea
- 1,2-bis(methylsulphonyl)-1-(2-chloroethyl)-2-[(methylamino)carbonyl]hydrazine
- 1-[(2-Chloro-4-methoxyphenoxy)methyl]-4-[(2,6-dichlorophenoxy)methyl]benzene
- 1-{3-[3-(4-chlorophenyl)propoxy]propyl}piperidine, hydrochloride
- 1-[(3R)-3-[4-amino-3-(4-fenossifenil)-1H-pirazolo[3,4 d]pirimidin-1-il]-1-piperidinil]-2-propen-1-one
- 1-(4-{4-amino-7-[1-(2-idrossietil)-1H- pirazol-4-il]tieno[3,2-c]piridin-3-il}fenil)-3-(3-fluorofenil)urea
- 1,5-(Butylimino)-1,5-dideoxy, D-glucitol
- 17-allylamino-17-demethoxygeldanamycin
- (-)-17-(cyclopropylmethyl)-3,14 ß-dihydroxy-4,5 a-epoxy-6ß-[N-methyl-trans-3-(3-furyl) acrylamido] morphinan hydrochloride
- 17-(Dimethylaminoethylamino)-17-demethoxygeldanamycin (after administration of adeno-associated viral vector encoding an inducible short hairpin RNA targeting claudin-5)
- 1-ciclopropil-3-[3-(5-morfolin-4-il-metil-1H-benzoimidazol-2-il)-1H-pirazol-4-il]-urea
- 1-deoxynojirimycin hydrochloride
- 1H-Benzimidazole-7-carboxamide, 2-[(2R)-2-methyl-2-pyrrolidinyl]
- (1-metil-2-nitro-1H-imidazolo-5-il)metil N,N'-bis(2-bromoetil) diamido fosfato
- (1R,2R)-octanoic acid[2-(2',3'-dihydro-benzo[1,4] dioxin-6'-yl).....-tartaric acid salt
- (1R,2S) 6-bromo-alpha-[2-(dimethylamino)ethyl]-2-methoxy-alpha-(1-naphthyl)-beta-phenyl-3-quinolineethanol
- 20-pentaeritritol poli (ossi-1,2-etanediil)-carbossimetil-glicinato-7-etil-10-idrossicamptotecina 10-[1,4'-bipiperidina]-1'-carbossilato
- 2,2'-{2-[(1R)-1-({[(2,5-diclorobenzoil)amino]acetil}amino)-3-metilbutil]-5-oxo-1,3,2-dioxaborolano-4,4-diyl}diacetato
- 2-(2-clorofenil)-4-[3-(dimetilamino)fenil]-5-metil-1H-pirazolo[4,3-c]piridin-3,6(2H, 5H)- dione
- 2,2-dimetilbutirrato sodico
- 2-[[3-({4-[(5-{2-[(3-Fluorofenil)amino]-2-ossoetil}-1H-pirazol-3-il)amino]-chinazolin-7-il}ossi)propil](etil)amino]etil diidrogeno fosfato triidrato
- 2,3,4,5 tetraidro-2,8-dimetil-5-[2-(6-metil-3-piridil)etil]-1H-pirido[4,3-b]indolo dicloridrato
- 2',3',5'-tri-O-acetiluridina
- 2-{4-[(5,6-diphenylpyrazin-2-yl)(isopropyl)amino]butoxy}-N-(methylsulfonyl)acetamide
- 2-[4-Methoxy-3-(2-m-tolyl-ethoxy)-benzoylamino]-indan-2-carboxylic acid
- 2-allil-1-[6-(1-idrossi-1-metiletil)piridin-2-il]-6-{[4-(4-metilpiperazin-1-il)fenil]amino}-1,2-diidro-3H-pirazolo [3,4-d]pirimidin-3-one
- [2-Cyano-3-cyclopropyl-3-hydroxy-N-(3-methyl-4-trifluoromethylphenyl)prop-2-enamide]
- 2-Iminobiotina
- 2-Methoxy-5-[(1Z)-2-(3,4,5-trimethoxyphenyl)ethenyl]-phenol
- 2-metossimetil-2-idrossimetil-1-azabiciclo[2.2.2]ottan-3-one
- (2R)-3-(2-hydroxymethylindanyl-4-oxy)-phenyl-4,4,4-trifluorobutane-1-sulfonate
- (2S)-2-{[(2R)-2-[({[3,3-dibutyl-7-(methylthio)-1,1-dioxido-5-phenyl-2,3,4,5-tetrahydro-1,2,5-benzothiadiazepin-8-yl]oxy}acetyl)amino]-2-(4-hydroxyphenyl)acetyl]amino}butanoic acid
- 2S 4R ketoconazole
- 3-(2-imidazo[1,2-b]piridazin-3-iletinil)-4-metil-N-[4-[(4-metil-1-piperazinil)metil]-3-(trifluorometil)fenil]- benzamide
- 3,4-diaminopyridine phosphate
- (3-[5-(2-fluoro-phenyl)-[1,2,4]oxadiazole-3-yl]-benzoic acid
- 3-methoxy-pregnelonone
- (3S)-3-{4-[7-(aminocarbonil)-2H-indazol-2-il] fenil} piperidina sale tosilato monoidrato
- 4-[123I] iodo-L-phenylalanine
- 4-[131I]iodo-L-phenylalanine
- 4-[2-(6-methylpyridin-2-yl)-5,6-dihydro-4H-pyrrolo[1,2-b]pyrazol-3-yl]-quinoline-6-carboxamide monohydrate
- 4-[3-(metilsulfonil)fenil]-1-propilpiperidina x HC1
- 4-(4-{[2-(4-chlorophenyl)-4,4-dimethylcyclohex-1-en-1-yl]methyl}piperazin-1-yl)-N-({3-nitro-4-[(tetrahydro-2H-pyran-4-ylmethyl)amino]phenyl}sulfonyl)-2-(1H-pyrrolo[2,3-b]pyridin-5-yloxy)benzamide
- 4,6,8-triidrossi-10-(3,7,11-trimetildodeca-2,6,10-trienil)-5,10-diidrodibenzo[b,e][1,4]diazepin-11-one
- 4,7,10,13,16,19-Docosahexaenoic acid
- 4-[[9-[(3S)-tetraidro-3-furanil]-8-[(2,4,6-trifluorofenil)amino]-9H-purin-2-il]amino]-trans-cicloesanolo
- 4-amino-5-oxo-4 (pyridinium-1-ylmethyl) prolina
- 4-amino-(6R,S)-5,6,7,8-tetrahydro-L-biopterin dihydrochloride
- 4-Amino-...-D-arabinofuranosyl]-...pyrimidinone
- 4-aminopyridine
- 4-benzil-2-naftalen-1-il-1,2,4-tiadiazolidin-3,5-dione
- 4-ethoxy-2-(piperazin-1-yl)-7-(pyridin-4-yl)-5H-pyrimido[5,4-b]indol
- 4-imino-1, 3-diazobicyclo-[3.1.0]-hexan-2-one
- 5-[1-(2,6-diclorobenzil)piperidina-4-ilmetossi] quinazolin-2,4-diamin dicloridrato
- 5-(2,6-Difluoro-phenoxy)-3(R,S)-{2(S)-[2(S)-(3-methoxycarbonyl-2(S)-{3-methyl-2(S)-[(quinoline-2-carbonyl)-amino]-butyrylamino}-propionylamino)-3-methyl-butyrylamino]-propionylamino}-4-oxo-pentanoic acid methyl ester
- 5-aminolevulinic acid hydrochloride
- 5'-CTG CCA CGT TCT CCT GC-(2' methoxy)A-(2' methoxy)C-(2' methoxy)C-3'
- 5-(ethylsulfonyl)-2-(naphthalen-2-yl)benzo[d]oxazole
- 5-methyl-pyridine-2-sulfonic acid {6-(2-hydroxy-ethoxy)-5-(2-methoxy-phenoxy)-2-...-amide sodium salt
- 5'-O-(trans-9"-octadecenoyl)-1-ß-D-arabinofuranosyl cytosine
- 5'-O-(trans-9''-ottadecenoil)-1-beta-D-2'deossi-2',2'-difluorocitidina
- 5(S)-(2'-hydroxy ethoxy)-20(S)-camptothecin
- 6-Cloro-2,3,4,9-tetraidro-1H-carbazol-1-carbossammide
- 6-etinil-1-(pentan-3-il)-1H-imidazo[4,5-b]pirazina-2(3H)-one
- (6R)-4, 5, 6, 7-tetrahydro-N6-propyl-2, 6-benzothiazolediamine dihydrochloride monohydrate
- 6-tioguanina (liquido orale)
- 7-beta-idrossi colesteril-3-beta-oleato
- 8-[4-(1-aminociclobutil)fenil]-9-fenil-1,2,4-triazolo[3,4-f][1,6]naftiridin-3(2H)-one monocloridrato
- 9-cis-retinil acetato