Designazioni Orfane per area geografica
- Lamotrigine
- Lanreotide acetate
- Laronidasa
- L-Asparaginase
- L-asparaginasi incapsulata in eritrociti
- L-asparaginasi pegilata ricombinante da Erwinia chrysanthemi
- Late Stage Human Motor Neutron Progenitors
- L carnitine
- L-cistein, L-leucil-L-alpha-glutamil-L-alpha-glutamil-L-lisil-L-lysylglycyl-L-asparaginyl-L-tyrosyl-L-valyl-L-valyl-L-threonyl-L-alpha-aspartil-L-istidil-S-[1-[(4-carboxycyclohexyl)metil]-2,5-diosso-3-pirrolidinile]-, complesso con emocianina da Megathura crenulata
- Lenalidomide
- Lentiviral vector containing the human Wiskott Aldrich syndrome protein gene
- Lepirudin
- Lestaurtinib
- Letermovir
- Leukocyte interleukin
- Leuprolide acetate
- Levamisolo idrochloruro
- Levodopa and Carbidopa (Gastroenteral use)
- Levofloxacin hemihydrate
- Levoglutamide
- Liarozole
- Linea cellulare di linfociti T citotossici umani MHC non-ristretti
- Lintuzumab
- Lipasi acida lisosomiale umana ricombinante
- Lipopolisaccaride di Ochrobactrum intermedium
- Liposomal daunorubicin
- Lisuride idrogenomaleato
- L-Lysine-N-acetyl-L-cysteinate
- Lomitapide
- L-threo-3,4-dihydroxyphenylserine
- Lucinactant
- Lurbinectedin
- Lutetium (177Lu)-N-[(4,7,10-Tricarboxymethyl-1,4,7,...Lthreonine-cyclic(2-7)disulfide










