Skip to
Languages:
FR
EN
ES
DE
IT
PT
The portal for rare diseases and orphan drugs
Orphanet index
Rare diseases are
rare
,
but
rare disease patients are
numerous
Homepage
Help
Contact us
Main menu :
Rare diseases
Orphan drugs
Expert centres
Diagnostic tests
Research and trials
Patient organisations
Professionals and institutions
Other information
Submenu :
Search
List of Orphan Designations
List of Orphan Drugs with MA
List of Substances
List of Drugs
Register / Update your activity
Navigation tree :
Homepage
Orphan drugs
Search
Print
Search by substance/trade name
Search by substance/trade name
Enter keywords
*
(*) mandatory field
Substance / Trade name
Search by substance/trade name
Other search option(s)
Search by disease name
Search by ATC category
Search by Sponsor / MA holder
10 Result(s)
6 Substances
;
4 Tradenames
Substances
C1-esterase inhibitor
Ecallantide
Human C1-inhibitor
Icatibant acetate
Recombinant human C1-inhibitor
Recombinant inhibitor of human plasma kallikrein
Tradenames
CINRYZE
FIRAZYR
KALBITOR
RUCONEST