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Adenoassociated virus vector (AAV) carrying a modified AAV serotype 2 backbone and coding sequence of human thymidine phosphorylase preceded by a human thyroxin-binding globulin promoter

   
  • INN (International Nonproprietary Name) : -
  • Code name : -
  • Chemical name or description : -
  • Type of product : Gene therapy product
  • Type of production : Biotechnology
  • Orphan designation : USA
    • Orphan designation  - USA

    • Diseases list
      • Mitochondrial neurogastrointestinal encephalomyopathy
    • Detailed information

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