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adeno-associated viral vector serotype 9 containing the human glucocerebrosidase gene

   
  • INN (International Nonproprietary Name) : -
  • Code name : -
  • Chemical name or description : adeno-associated viral vector serotype 9 containing the human glucocerebrosidase gene
  • Type of product : Gene therapy product
  • Type of production : Biotechnology
  • Orphan designation : Europe
    • Orphan designation  - Europe

    • Diseases list
      • Gaucher disease type 1
      • Gaucher disease type 2
      • Gaucher disease type 3
      • Gaucher disease-ophthalmoplegia-cardiovascular calcification syndrome
    • Detailed information

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