Orphan Designations by geographical area
- Paclitaxel
- Paclitaxel (aqueous gel)
- Paclitaxel (liposomal)
- Paclitaxel (micellar)
- Pafuramidine maleate
- Palifosfamide
- Pancreatic enzymes (cross linked enzyme crystal lipase, protease, amylase)
- Panobinostat
- Panobinostat lactate
- Paquinimod
- Para-aminosalicylic acid
- Parathyroid hormone (1-34) transglutaminase fusion protein fibrin matrix complex
- Pasireotide diaspartate
- Patupilone (Epothilone B)
- Pegademase bovine
- Pegaspargase
- Pegvisomant
- Pegylated arginine deiminase
- Pegylated B-domain-deleted sequence-modified recombinant human factor VIII
- Pegylated carboxyhaemoglobin
- Pegylated L-asparaginase
- Pegylated proline-interferon alpha-2b
- Pegylated recombinant Erwinia chrysanthemi L-asparaginase
- Pegylated recombinant factor VIIa
- Pegylated recombinant factor VIII
- Pegylated recombinant human factor IX
- Pegylated recombinant phenylalanine ammonia lyase
- Pemetrexed disodium
- Pentamidine isethionate
- Peptide 144 TGF-beta1-inhibitor (TSLDASIIWAMMQN)
- Peptides mimicking antigen receptors on autoimmune B cells and autoimmune T cells associated with myasthenia gravis
- Peptidomimetic analog of hexarelin
- Peretinoin
- Perifosine
- Phenylalanine ammonia lyase
- Phenylephrine Hydrochloride
- Picoplatin
- Pirfenidone
- Plerixafor
- Plevitrexed
- Plitidepsin
- Polihexanide
- Poloxamer 188
- Polyinosine-polycytidylic acid coupled with the polycationic polyethyleneimine
- Pomalidomide
- Porcine Fetal Neural Gabaergic Cells And/Or Precursors Aseptically Prepared And Coated With Anti-Mhc-1 Ab For Intracerebral Implantation
- Porcine Fetal Neural Gabaergic Cells And/Or Precursors Aseptically Prepared For Intracerebral Implantation For Huntington'S Disease
- Porfimer sodium (for use with photodynamic therapy)
- Potassium iodide oral solution
- Pralatrexate
- Prasterone
- Pravastatin / zoledronic acid
- Progesterone
- Pseudomonas exotoxin (domains II/III)-Interleukin 13 chimeric protein
- Pulmonary surfactant replacement, porcine
- Pyr-His-Trp-Ser-Tyr-D-Lys(doxorubicinylglutarate)-Leu-Arg-Pro-Gly-NH2, acetate salt
- Pyridoxalated hemoglobin polyoxyethylene
