Orphan Designations by geographical area
- Tacrolimus
- Tafamidis
- Tafamidis meglumine
- Talactoferrinum alfa
- Talampanel
- Talarozole
- Taliglucerase alfa
- Tamibarotene
- Tasimelteon
- Tazarotene
- T-Cell Depleted Stem Cell Enriched Cellular Product From Peripheal Blood Stem Cells
- Teduglutide
- Temocillin sodium
- Temozolomide
- Temsirolimus
- Terguride
- Tesetaxel
- Tetrahydrobiopterin
- Thalidomide
- Thiotepa
- Thymalfasin
- Thyrotropin alpha
- Tinidazole
- Tiopronine
- Tipifarnib
- Tissue Repair Cells Obtained From Autologous Bone Marrow Expanded Ex Vivo With A Cell Production System
- Titanium dioxide and bisoctrizole
- Tobramycin (inhalation powder)
- Tobramycin (inhalation solution)
- Tobramycin (inhalation use)
- Tobramycin (liposomal)
- Topotecan hydrochloride (liposomal)
- Tosedostat
- Tositumomab
- Trabectedin
- Trabedersen
- Tralokinumab
- Tranilast
- (-)-trans-3-(5,6-dihydro-4H-pyrrolo[3,2,1-ij]quinolin-1yl)-4-(1H-indol-3-yl) pyrrolidine-2, 5-dione
- Trastuzumab
- Treosulfan
- Treprostinil diethanolamine
- Treprostinil diethanolamine (oral use)
- Treprostinil sodium
- Treprostinil sodium (inhalation use)
- Tretazicar
- Trientine dihydrochloride
- Triheptanoin
- Trimetrexate glucuronate
- Type I native bovine skin collagen
- Tyrosine kinase inhibitor










