Orphan Designations by geographical area
- Vaccinia GM-CSF/TK-deactivated virus
- Vandetanib
- Vapreotide
- Vascular endothelial growth factor-D gene in an adenoviral vector for use with a collagen collar
- Vasoactive intestinal peptide
- Vatreptacog alfa (activated)
- Velaglucerase alfa
- Veliparib
- Veltuzumab
- Verteporfine
- Vincaleukoblastin-23-oic acid, O4-deacetyl-2-[(2-mercaptoethoxy)carbonyl]hydrazide, disulfide with N-[4-[[(2-amino-3,4-dihydro-4-oxo-6-pteridinyl)methyl]amino]benzoyl]-L-gamma-glutamyl-L-alpha-aspartyl-L-arginyl-L-alpha-aspartyl-L-alpha-aspartyl-L-cysteine
- Vincristine sulfate liposomes
- Viral vector containing DNA encoding the human SMN protein
- Voclosporin
- Vorinostat
- Vosaroxin










