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Marketing authorisation with orphan designation - Europe
- Tradename: CERDELGA
- ATC code : A16AX10
- EU Number: EU/1/14/974
- MA date : 19/01/2015
- MA holder: GENZYME EUROPE B.V.
- European Public Assessment Report
Therapeutic indication
Long-term treatment of adult patients with Gaucher disease type 1 (GD1), who are CYP2D6 poor metabolisers (PMs), intermediate metabolisers (IMs) or extensive metabolisers (EMs).
Diseases list
Appraisal/reimbursement
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