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Orphan designation withdrawn - Europe

  • Substance: 505 amino acid protein, corresponding to amino acids 2-506 of the wild type human histidyl-tRNA synthetase
  • ATC code : -
  • EU Number: EU/3/15/1448
  • Designation date : 12/02/2015
  • Sponsor of orphan designation : VOISIN CONSULTING S.A.R.L.
  • Summary of Opinion


Treatment of facioscapulohumeral muscular dystrophy.

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