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Orphan designation - Europe

  • Substance: adeno-associated viral vector serotype 9 containing the human glucocerebrosidase gene
  • ATC code : -
  • EU Number: EU/3/15/1468
  • Designation date : 19/03/2015
  • Sponsor of orphan designation : GAUCHERS ASSOCIATION
  • Summary of Opinion


Treatment of Gaucher disease

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