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Orphan designation - Europe

  • Substance: Adenovirus associated viral vector serotype 5 containing the human RPE65 gene
  • ATC code : -
  • EU Number: EU/3/15/1577
  • Designation date : 11/11/2015
  • Sponsor of orphan designation : ATHENA VISION LTD
  • Summary of Opinion

Designation

Treatment of Leber's congenital amaurosis.

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