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Orphan designation - Europe

  • Substance: Adenovirus associated viral vector serotype 8 containing the human CNGB3 gene
  • ATC code : -
  • EU Number: EU/3/15/1578
  • Designation date : 11/11/2015
  • Sponsor of orphan designation : ATHENA VISION LTD
  • Summary of Opinion


Treatment of achromatopsia caused by mutations in the CNGB3 gene.

Diseases list

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