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Orphan designation - Europe

  • Substance: Adeno-associated viral vector containing the human factor IX gene
  • ATC code : -
  • EU Number: EU/3/15/1599
  • Designation date : 14/12/2015
  • Sponsor of orphan designation : PHARMA GATEWAY AB
  • Summary of Opinion

Designation

Treatment of haemophilia B

Diseases list

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