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Orphan designation - Europe

  • Substance: adenovirus associated viral vector serotype 5 containing the RPGR gene
  • ATC code : -
  • EU Number: EU/3/16/1715
  • Designation date : 29/08/2016
  • Sponsor of orphan designation : MEIRAGTX LIMITED
  • Summary of Opinion


Treatment of retinitis pigmentosa.

Diseases list

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