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Orphan designation - Europe

  • Substance: Apolipotrotein C-III antisense oligonucleotide
  • ATC code : -
  • EU Number: EU/3/16/1711
  • Designation date : 14/07/2016
  • Sponsor of orphan designation : AKCEA THERAPEUTICS IRELAND LIMITED
  • Summary of Opinion


Treatment of familial partial lipodystrophy.

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