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Orphan designation - Europe

  • Substance: Adeno-associated viral vector serotype 9 containing the human mini-dystrophin gene
  • ATC code : -
  • EU Number: EU/3/16/1716
  • Designation date : 29/08/2016
  • Sponsor of orphan designation : ADVANCED BIOTHERAPEUTICS CONSULTING SARL
  • Summary of Opinion

Designation

Treatment of Duchenne muscular dystrophy.

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