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Orphan designation - Europe
- Substance: Allogeneic cultured postnatal thymus-derived tissue
- ATC code : -
- EU Number: EU/3/19/2137
- Designation date : 26/02/2019
- Sponsor of orphan designation : ENZYVANT THERAPEUTICS IRELAND LIMITED
- Summary of Opinion
Designation
Treatment of severe combined immunodeficiency due to FOXN1 deficiency.
Diseases list
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