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Orphan designation - Europe

  • Substance: Allogeneic cultured postnatal thymus-derived tissue
  • ATC code : -
  • EU Number: EU/3/19/2137
  • Designation date : 26/02/2019
  • Sponsor of orphan designation : ENZYVANT THERAPEUTICS IRELAND LIMITED
  • Summary of Opinion


Treatment of severe combined immunodeficiency due to FOXN1 deficiency.

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