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Orphan designation - Europe

  • Substance: Setmelanotide
  • ATC code : -
  • EU Number: EU/3/19/2192
  • Designation date : 21/08/2019
  • Sponsor of orphan designation : RHYTHM PHARMACEUTICALS NETHERLANDS B.V.
  • Summary of Opinion


Treatment of Bardet-Biedl syndrome.

Diseases list

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