Orphanet: Search for an orphan drug

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    • Marketing authorisation withdrawn  - Europe

    • Diseases list
      • Cryopyrin-associated periodic syndrome
    • Detailed information
    • Marketing authorization with orphan designation  - USA

    • Diseases list
      • CINCA syndrome
      • Muckle-Wells syndrome
      • Familial cold urticaria
    • Detailed information

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