Orphanet: Search for an orphan drug

Search for an orphan drug

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    • Marketing authorization without orphan designation  - Europe

    • Diseases list
      • Cryopyrin-associated periodic syndrome
      • Systemic-onset juvenile idiopathic arthritis
    • Detailed information
    • Marketing authorization with orphan designation  - USA

    • Diseases list
      • Muckle-Wells syndrome
      • Familial cold urticaria
      • Familial Mediterranean fever
      • Systemic-onset juvenile idiopathic arthritis
      • Hyperimmunoglobulinemia D with periodic fever
      • Tumor necrosis factor receptor 1 associated periodic syndrome
    • Detailed information

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