Orphanet: Search for an orphan drug

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  • INN (International Nonproprietary Name) : -
  • Code name : -
  • Chemical name or description : -
  • Type of product : Ingredient/substance
  • Type of production : Biotechnology
  • Orphan designation : EuropeUSA
    • Orphan designation  - USA

    • Diseases list
      • Refractory anemia
      • Aregenerative anemia
      • Myelodysplastic syndrome
      • Refractory anemia with excess blasts
      • Unclassified myelodysplastic syndrome
      • Acquired idiopathic sideroblastic anemia
      • Refractory cytopenia with multilineage dysplasia
      • Myelodysplastic syndrome associated with isolated del(5q) chromosome abnormality
    • Detailed information
    • Orphan designation  - USA

    • Diseases list
      • Acute myeloid leukemia
      • Acute erythroid leukemia
      • Acute promyelocytic leukemia
      • Acute myelomonocytic leukemia
      • Acute megakaryoblastic leukemia
      • Acute panmyelosis with myelofibrosis
      • Acute myeloid leukaemia with myelodysplasia-related features
      • Therapy related acute myeloid leukemia and myelodysplastic syndrome
    • Detailed information

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