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Autologous haematopoietic stem cells transduced with lentiviral vector Lenti-D encoding the human ABCD1 cDNA (elivaldogene autotemcel)

   Skysona   
  • INN (International Nonproprietary Name) : elivaldogene autotemcel
  • Code name : -
  • Chemical name or description : Autologous haematopoietic stem cells transduced with lentiviral vector Lenti-D encoding the human ABCD1 cDNA (elivaldogene autotemcel)
  • Type of product : Gene therapy product
  • Type of production : Biotechnology
  • Orphan designation : Europe
    • Marketing authorization with orphan designation  - Europe

    • Diseases list
      • X-linked adrenoleukodystrophy
    • Detailed information

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