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Triheptanoin
DOJOLVI- INN (International Nonproprietary Name) : -
- Code name : UX007
- Chemical name or description : -
- Type of product : Ingredient/substance
- Type of production : Synthetic / extractive chemistry
- Orphan designation :
Orphan designation - Europe
- Diseases list
- Very long chain acyl-CoA dehydrogenase deficiency
- Detailed information
Orphan designation - Europe
- Diseases list
- Mitochondrial trifunctional protein deficiency
- Detailed information
Orphan designation - Europe
- Diseases list
- Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
- Detailed information
Orphan designation - Europe
- Diseases list
- Glycogen storage disease due to muscle glycogen phosphorylase deficiency
- Detailed information
Orphan designation - Europe
- Diseases list
- Carnitine palmitoyltransferase II deficiency
- Detailed information
Orphan designation - Europe
- Diseases list
- Carnitine-acylcarnitine translocase deficiency
- Detailed information
Orphan designation - Europe
- Diseases list
- Carnitine palmitoyl transferase 1A deficiency
- Detailed information
Orphan designation withdrawn/expired - Europe
- Diseases list
- Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
- Detailed information
Orphan designation withdrawn/expired - Europe
- Diseases list
- Very long chain acyl-CoA dehydrogenase deficiency
- Detailed information
Orphan designation withdrawn/expired - Europe
- Diseases list
- Classic glucose transporter type 1 deficiency syndrome
- Detailed information
Orphan designation - USA
- Diseases list
- Classic glucose transporter type 1 deficiency syndrome
- Detailed information
Additional information
Research on this medical product
Appraisal/reimbursement
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