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Venglustat
- INN (International Nonproprietary Name) : venglustat
- Code name : GZ/SAR402671
- Chemical name or description
: (3S)-1-azabicyclo[2.2.2]oct-3-yl{2-[2-(4-fluorophenyl)-1,3-t
hiazol-4-yl]propan-2-yl}carbamate
- Type of product : Ingredient/substance
- Type of production : Synthetic / extractive chemistry
- Orphan designation :
Orphan designation - Europe
- Diseases list
- Fabry disease
- Detailed information
Orphan designation - Europe
- Diseases list
- GM2 gangliosidosis
- Detailed information
Orphan designation - Europe
- Diseases list
- Gaucher disease
- Detailed information
Orphan designation withdrawn/expired - Europe
- Diseases list
- Autosomal dominant polycystic kidney disease
- Detailed information
Orphan designation - USA
- Diseases list
- Gaucher disease
- Detailed information
Orphan designation - USA
- Diseases list
- Fabry disease
- Detailed information
Additional information
Research on this medical product
Appraisal/reimbursement
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