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Lentiviral vector containing the human liver and erythroid pyruvate kinase (PKLR) gene

  • INN (International Nonproprietary Name) : -
  • Code name : RP-L301
  • Chemical name or description : -
  • Type of product : Gene therapy product
  • Type of production : Biotechnology
  • Orphan designation :
    • Orphan designation  - Europe

    • Diseases list
      • Hemolytic anemia due to red cell pyruvate kinase deficiency
    • Detailed information

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