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2'-O-methyl phosphorothioate RNA oligonucleotide, 5'-m5CUGm5CUGm5CUGm5CUGm5CUGm5CUGm5CUG-3'

  • INN (International Nonproprietary Name) : -
  • Code name : VO659
  • Chemical name or description : -
  • Type of product : Gene therapy product
  • Type of production : Synthetic / extractive chemistry
  • Orphan designation :
    • Orphan designation  - Europe

    • Diseases list
      • Spinocerebellar ataxia type 1
      • Spinocerebellar ataxia type 3
    • Detailed information

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