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2'-O-methyl phosphorothioate RNA oligonucleotide, 5'-m5CUGm5CUGm5CUGm5CUGm5CUGm5CUGm5CUG-3'
- INN (International Nonproprietary Name) : -
- Code name : VO659
- Chemical name or description : -
- Type of product : Gene therapy product
- Type of production : Synthetic / extractive chemistry
- Orphan designation :
Orphan designation - Europe
- Diseases list
- Huntington disease
- Detailed information
Orphan designation - Europe
- Diseases list
- Spinocerebellar ataxia type 1
- Spinocerebellar ataxia type 3
- Detailed information
Additional information
Research on this medical product
Appraisal/reimbursement
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