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adeno-associated viral vector serotype 9 containing the human glucocerebrosidase gene
- INN (International Nonproprietary Name) : -
- Code name : -
- Chemical name or description : adeno-associated viral vector serotype 9 containing the human glucocerebrosidase gene
- Type of product : Gene therapy product
- Type of production : Biotechnology
- Orphan designation :
Orphan designation withdrawn/expired - Europe
- Diseases list
- Gaucher disease type 1
- Gaucher disease type 2
- Gaucher disease type 3
- Gaucher disease-ophthalmoplegia-cardiovascular calcification syndrome
- Detailed information
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