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PEGylated peptide inhibitor of complement C3
- INN (International Nonproprietary Name) : pegcetacoplan
- Code name : APL-2
- Chemical name or description
: Poly(oxy-1,2-ethanediyl),.alpha.-hydro-.omega.-hydroxy-,15,1
5'-diester with N-acetyl-L-isoleucyl-L-cysteinyl-L-valyl-1-methyl-L-tryptoph yl-L-glutaminyl-L-.alpha.-aspartyl-L-tryptophylglycyl-L-alan yl-L-histidyl-L-arginyl-L-cysteinyl-L-threonyl-2-[2-(2-amino
ethoxy)ethoxy]acetyl-N6-carboxy-L-lysinamide cyclic (2.fwdarw.12)-(disulfide)
- Type of product : Ingredient/substance
- Type of production : Synthetic / extractive chemistry
- Orphan designation :
Orphan designation - Europe
- Diseases list
- Paroxysmal nocturnal hemoglobinuria
- Detailed information
Orphan designation - Europe
- Diseases list
- C3 glomerulopathy
- Detailed information
Orphan designation - USA
- Diseases list
- C3 glomerulopathy
- Detailed information
Orphan designation - USA
- Diseases list
- Autoimmune hemolytic anemia
- Detailed information
Orphan designation - USA
- Diseases list
- Paroxysmal nocturnal hemoglobinuria
- Detailed information
Additional information
Research on this medical product
Appraisal/reimbursement
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