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Combination of three adeno-associated viral vectors of serotype 8 containing the 5'-, the body- and the 3'- coding sequences of human CEP290 fused to inteins
- INN (International Nonproprietary Name) : -
- Code name : -
- Chemical name or description : -
- Type of product : Gene therapy product
- Type of production : Biotechnology
- Orphan designation : Europe
Orphan designation - Europe
- Diseases list
- Inherited retinal disorder
- Detailed information
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