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CYSTADANE

Betaine anhydrous   
    • Marketing authorization without orphan designation  - Europe

    • Diseases list
      • Classic homocystinuria
      • Methylmalonic acidemia with homocystinuria
      • Homocystinuria without methylmalonic aciduria
      • Homocystinuria due to methylene tetrahydrofolate reductase deficiency
    • Detailed information
    • Marketing authorization with orphan designation  - USA

    • Diseases list
      • Classic homocystinuria
      • Methylcobalamin deficiency type cblE
      • Methylcobalamin deficiency type cblG
      • Methylmalonic acidemia with homocystinuria
      • Homocystinuria due to methylene tetrahydrofolate reductase deficiency
    • Detailed information

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