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CYSTADANE
Betaine anhydrousMarketing authorisation without orphan designation - Europe
- Diseases list
- Methylmalonic acidemia with homocystinuria
- Homocystinuria without methylmalonic aciduria
- Homocystinuria due to cystathionine beta-synthase deficiency
- Homocystinuria due to methylene tetrahydrofolate reductase deficiency
- Detailed information
Marketing authorisation with orphan designation - USA
- Diseases list
- Methylcobalamin deficiency type cblE
- Methylcobalamin deficiency type cblG
- Methylmalonic acidemia with homocystinuria
- Homocystinuria due to cystathionine beta-synthase deficiency
- Homocystinuria due to methylene tetrahydrofolate reductase deficiency
- Detailed information
Additional information
Research on this medical product
Appraisal/reimbursement
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