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Betaine anhydrous

  • INN (International Nonproprietary Name) : Betaine anhydrous
  • Code name : -
  • Chemical name or description : -
  • Type of product : Ingredient/substance
  • Type of production : Synthetic / extractive chemistry
  • Orphan designation :
    • Orphan designation withdrawn/expired  - Europe

    • Diseases list
      • Homocystinuria due to cystathionine beta-synthase deficiency
    • Detailed information
    • Orphan designation  - USA

    • Diseases list
      • Methylcobalamin deficiency type cblE
      • Methylcobalamin deficiency type cblG
      • Methylmalonic acidemia with homocystinuria
      • Homocystinuria due to cystathionine beta-synthase deficiency
      • Homocystinuria due to methylene tetrahydrofolate reductase deficiency
    • Detailed information

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