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- INN (International Nonproprietary Name) : Betaine anhydrous
- Code name : -
- Chemical name or description : -
- Type of product : Ingredient/substance
- Type of production : Synthetic / extractive chemistry
- Orphan designation :
Orphan designation withdrawn/expired - Europe
- Diseases list
- Homocystinuria due to cystathionine beta-synthase deficiency
- Detailed information
Orphan designation - USA
- Diseases list
- Methylcobalamin deficiency type cblE
- Methylcobalamin deficiency type cblG
- Methylmalonic acidemia with homocystinuria
- Homocystinuria due to cystathionine beta-synthase deficiency
- Homocystinuria due to methylene tetrahydrofolate reductase deficiency
- Detailed information
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