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    • Marketing authorization without orphan designation  - France

    • Diseases list
      • Omenn syndrome
      • Kawasaki disease
      • Reticular dysgenesis
      • Guillain-Barré syndrome
      • Immune thrombocytopenia
      • X-linked agammaglobulinemia
      • Autosomal agammaglobulinemia
      • Common variable immunodeficiency
      • B-cell chronic lymphocytic leukemia
      • Combined immunodeficiency due to ZAP70 deficiency
      • Immunodeficiency by defective expression of MHC class II
      • Severe combined immunodeficiency due to DCLRE1C deficiency
      • T-B+ severe combined immunodeficiency due to JAK3 deficiency
      • T-B+ severe combined immunodeficiency due to gamma chain deficiency
      • Severe combined immunodeficiency due to adenosine deaminase deficiency
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