Search for an orphan drug

* (*) mandatory field

Other search option(s)

Orphan designation - Europe

  • Substance: Cholic acid
  • ATC code : -
  • EU Number: EU/3/09/683
  • Designation date : 28/10/2009
  • Sponsor of orphan designation : RETROPHIN EUROPE LTD
  • Summary of Opinion


Treatment of inborn errors of primary bile acid synthesis responsive to treatment with cholic acid.

The documents contained in this web site are presented for information purposes only. The material is in no way intended to replace professional medical care by a qualified specialist and should not be used as a basis for diagnosis or treatment.