Search for an orphan drug
Other search option(s)
27 Result(s)
Substance(s)
- (3beta,24S)-25,25,25-trifluoro-3-methyl-26,27-dinorergost-5-ene-3,24-diol
- 2'-O-methyl phosphorothioate RNA oligonucleotide, 5'-m5CUGm5CUGm5CUGm5CUGm5CUGm5CUGm5CUG-3'
- 2,3,4,5 tetrahydro-2,8-dimethyl-5-[2-(6-methyl-3-pyridinyl)ethyl]-1H-pyrido[4,3-b]indole dihydrochloride
- 2-(3,7-Dimethyl-octa-2, 6-dienyl)-6-ethylamino-3-hydroxy-5-pentyl-[1,4]benzoquinone
- 5,7-dichloro-2-dimethylaminomethyl-8-hydroxyquinoline hydrochloride
- 5,7-dichloro-2-methylaminomethyl-8-hydroxyquinolone hydrochloride
- 5-bromo-N-(prop-2-yn-1-yl)-2-(1H-1,2,4-triazol-1-yl) pyrimidine-4,6-diamine
- AASSGVSTPGSAGHDIITEQPRS (P42 peptide)
- Adeno-associated viral vector serotype 5 encoding a microRNA targeted to human huntingtin gene
- Adeno-associated viral vector serotype rh10 containing the human cholesterol 24-hydroxylase gene
- Carbenoxolone
- Cysteamine bitartrate
- Deutetrabenazine
- Ethyl eicosopentaenoate
- Humanized recombinant immunoglobulin G (IgG) 4 monoclonal antibody against C1q
- Lithium citrate tetrahydrate (in reverse-micelle formulation)
- Phosphodiesterase 10 (PDE10) Inhibitor
- Plasmid encoding a rabies virus glycoprotein tag & lysosome-associated membrane glycoprotein 2 fusion protein gene and a mutant huntingtin small interfering RNA
- Porcine fetal neural gabaergic cells and/or precursors aseptically prepared and coated with anti-Mhc-1 Ab for intracerebral implantation
- Porcine fetal neural gabaergic cells and/or precursors aseptically prepared for intracerebral implantation for Huntington's disease
- Pridopidine hydrochloride
- Selisistat
- Tominersen
- Tyr-Gly-Arg-Lys-Lys-Arg-Arg-Gln-Arg-Arg-Gly-Gly-Asp-Leu-Leu-Pro-Arg-Gly-Ser
- Valbenazine
- phenol, 4-[2-(aminomethyl)-4-thiazolyl]-2,6-bis(1,1-dimethylethyl) monohydrochloride