Vyhledat léčivý přípravek pro vzácné onemocnění
Další možnosti vyhledávání
79 Výsledků
Účinné látky
- (2S)-2-{[(2R)-2-[({[3,3-dibutyl-7-(methylthio)-1,1-dioxido-5-phenyl-2,3,4,5-tetrahydro-1,2,5-benzothiadiazepin-8-yl]oxy}acetyl)amino]-2-(4-hydroxyphenyl)acetyl]amino}butanoic acid
- (R)-3-(2,3-dihydroxypropyl)-6-fluoro-5-(2-fluoro-4-iodophenylamino)-8-methylpyrido[2,3-d]pyrimidine-4,7(3H,8H)-dione
- 3-(((1S,2S,3R)-2,3-difluoro-1-hydroxy-7-(methylsulfonyl)-2,3-dihydro-1H-inden-4-yl)oxy)-5-fluorobenzonitrile
- Acetylleucine
- Adenoviral vector containing human p53 gene
- Afatinib
- Autologous CD34+ cells transduced with the W1.6_hWASP_WPRE lentiviral vector
- Autologous CD34+ cells transfected with a lentiviral vector containing codon optimised RPS19 gene
- Autologous CD34+ cells transfected with lentiviral vector containing the Wiskott-Aldrich syndrome protein gene
- Autologous CD34+ enriched cells transduced with a self-inactivating lentiviral vector containing the codon-optimized RPS19 gene
- Bacterial lipase
- Betamethasone
- Cannabidiol
- Celecoxib
- Dexamethasone sodium phosphate encapsulated in human erythrocytes
- Eflornithine
- Eflornithine hydrochloride
- Eflornithine in combination with sulindac
- Eicosapentaenoic acid
- Entospletinib
- Everolimus
- Ganaxolone
- Gefitinib
- Glasdegib
- Itraconazole
- Lentiviral vector carrying the Fanconi anaemia-A (FANCA) gene
- Lentiviral vector containing the human Wiskott Aldrich syndrome protein gene
- Liprotamase
- Lithium carbonate
- Maralixibat chloride
- Mirdametinib
- N-[6-(cis-2,6-Dimethylmorpholin-4-yl)pyridine-3-yl]-2-methyl-4'-(trifluoromethoxy)[1,1'- biphenyl]-3-carboxamide
- N-hydroxy-4-(3-methyl-2-(S)-phenyl-butyrylamino)benzamide
- Nitisinone
- Patidegib
- Pracinostat
- Pralsetinib
- Propranolol hydrochloride
- Recombinant human dyskerin
- Recombinant microbial lipase
- Salmonella enterica, subsp. enterica, serovar Typhimurium, strain YS1646, live
- Selpercatinib
- Selumetinib
- Sirolimus
- Trineumin
- Valproic acid, sodium
- [5,10,15,20-tetrakis(4-carboxyphenyl)-21H,23H-porphine]manganese(III) chloride
Obchodní název
- AFINITOR
- AZACITIDINE ACCORD
- AZACITIDINE BETAPHARM
- AZACITIDINE CELGENE
- CAMPTO
- CELEBREX
- COMETRIQ
- DAURISMO
- ELOXATINE
- ENDOBULINE
- EPIDIOLEX
- EPIDYOLEX
- ERIVEDGE
- GAMMAGARD
- GAVRETO
- HYFTOR
- Jemperli
- KOSELUGO
- Livmarli
- NITISINONE MDK
- NITYR
- OCTAGAM
- ONSENAL
- ORFADIN
- RETEVMO
- RETSEVMO
- SANDOGLOBULINE
- VEDROP
- VENCLEXTA
- VOTUBIA
- Welireg
- XOSPATA