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38 Result(s)
Substance(s)
- 6'-(R)-methyl-5-O-(5-amino-5,6-dideoxy-alpha-L-talofuranosyl)-paromamine sulfate
- Adeno-associated viral vector containing the human ARSB gene
- Adeno-associated viral vector containing the human alpha-N-acetylglucosaminidase gene
- Adeno-associated viral vector serotype 2/6 encoding zinc-finger nucleases and the human alpha L-iduronidase gene
- Adeno-associated viral vector serotype 2/6 encoding zinc-finger nucleases and the human iduronate 2-sulfatase gene
- Adeno-associated viral vector serotype 9 containing the human N-acetylglucosaminidase alpha gene
- Adeno-associated viral vector serotype 9 containing the human iduronate-2-sulfatase gene
- Adeno-associated viral vector serotype 9 containing the human sulfamidase gene
- Adeno-associated viral vector serotype rh.10 carrying the human N-sulfoglucosamine sulfohydrolase cDNA
- Adenovirus-associated viral vector serotype 10 carrying the human N-sulfoglucosamine sulfohydrolase and sulfatase modifying factor 1 cDNAs
- Autologous CD34+ cells transduced with a lentiviral vector containing the human SGSH gene
- Chemically modified human recombinant sulfamidase
- Chimeric fusion protein of recombinant human alpha-N-acetylglucosaminidase and human insulin-like growth factor 2
- Elosulfase alfa
- Galsulfase
- Genistein sodium salt dihydrate
- Humanised IGg1 monoclonal antibody targeting human transferrin receptor conjugated to human iduronate-2-sulfatase
- Idursulfase
- Laronidase
- N-terminal hexaglutamine-tagged recombinant human N-acetylgalactosamine-6-sulfate sulfatase
- Odiparcil
- Recombinant AAV9 expressing human alpha-N-acetylglucosaminidase
- Recombinant AAV9 expressing human sulfoglucosamine sulfohydrolase
- Recombinant adeno-associated viral vector serotype 9 containing human iduronidase gene
- Recombinant adeno-associated viral vector serotype 9 containing the human N-alpha-acetylglucosaminidase gene
- Recombinant human alpha-N-acetylglucosaminidase
- Recombinant human beta-glucuronidase
- Recombinant human heparan-N-sulfatase
- Recombinant human insulin receptor monoclonal antibody-fused iduronate 2-sulfatase ( HIRMAb-IDS)
- Recombinant human insulin receptor monoclonal antibody-fused-alpha-L-iduronidase
- Self-complementary adeno-associated viral vector serotype 9 containing the SGSH gene
- adeno-associated viral vector serotype 9 containing the human HGSNAT gene
- autologous CD34+ haematopoietic stem and progenitor cells genetically modified with the lentiviral vector IDUA LV, encoding for the alpha-L-iduronidase cDNA