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18 Result(s)
Substance(s)
- 5-[1-(2,6-dichlorobenzyl)piperidin-4-ylmethoxy]quinazoline-2,4-diamine dihydrochloride
- Adeno-associated viral vector serotype 9 containing the human SMN gene
- Adeno-associated viral vector serotype hu68 containing the human SMN1 gene
- Adeno-associated virus serotype 9 expressing the human Survival Motor Neuron gene
- Allogeneic motor neuron progenitor cells derived from human embryonic stem cells
- Antisense oligonucleotide targeted to the SMN2 gene
- Glycerol phenylbutyrate
- Human anti-promyostatin monoclonal antibody
- Late Stage Human Motor Neutron Progenitors
- Olesoxime
- Reldesemtiv
- Risdiplam
- Sodium phenylbutyrate
- Sodium valproate
- Viral vector containing DNA encoding the human SMN protein
- branaplam