Search for an orphan drug
121 Result(s)
- ((S)-3-(1-Cyclopentyl-5-(2-(trifluoromethyl)phenyl)-1H-pyrazole-3-carboxamido)-5-(3,3-difluoropiperidin-1-yl)pentanoic acid hydrochloride)
- (1'R,6'R)-3-(benzylamine)-6-hydroxy-3'-methyl-4-pentyl-6'-(prop-1-en-2-yl)-[1,1'-bi(cyclohexane)]-2',3,6-triene-2,5-dione
- (S)-N-(5-(1-(3-ethoxy-4-methoxyphenyl)-2-(methylsulfonyl)ethyl)-4,6-dioxo-5,6-dihydro-4H-thieno[3,4-c]pyrrol-1-yl)acetamide
- 2-(2-chlorophenyl)-4-[3-(dimethylamino)phenyl]-5-methyl-1H-pyrazolo[4,3-c]pyridine-3,6(2H,5H)-dione
- 2-[1-(3-{6-[(1E)-(hydroxyimino)methyl]-5-methyl-4-oxo-7-propyl-3H,4H-pyrrolo[2,1-f][1,2,4]triazin-2-yl}-4-propoxybenzenesulfonyl)piperidin-4-yl]ethyl nitrate
- 2-[4-Methoxy-3-(2-m-tolyl-ethoxy)-benzoylamino]-indan-2-carboxylic acid
- 2-{2,6-Dichloro-3-[(2,2-dimethyl-propionylamino)-methyl]-phenylamino}-6-(2,2-difluoroethoxy)-1-methyl-1H-benzoimidazole-5-carboxylic acid (trans-4-trifluoromethylcyclohexyl)-amide, hydrogensulfate
- 5'-As Cs As Ts Cs As Gs Ts Cs Ts Gs As Us As As Gs Cs Ts As-3'
- 5-Arylnicotinamide ABCA1 inducer
- Abetimus sodium
- Adalimumab
- Adult human bone-marrow-derived, ex-vivo-expanded, pooled allogeneic mesenchymal stromal cells
- Apremilast
- Autologous adipose tissue-derived mesenchymal stem cells
- Autologous bone marrow-derived mononuclear cell fraction
- Avacopan
- Aviptadil
- Bardoxolone methyl
- Begelomab
- Belimumab
- Birtamimab
- Bosentan
- Brodalumab
- Canakinumab
- Caprine hyperimmune serum against HIV lysate
- Carboxy pyrrolidine hexanoyl pyrrolidine carboxylate
- Chimeric fibril-reactive IgG1k monoclonal antibody 11-1F4
- Colchicine
- Danicopan
- Daratumumab
- Eculizumab
- Efzofitimod
- Eprodisate
- Fresolimumab
- Fusion protein composed of the first 2 immunoglobulin-like domains of the human roundabout guidance receptor 2 fused to a human IgG1 crystallised fragment
- Gevokizumab
- Glucagon like peptide-1 (GLP-1) Elastin like peptide (ELP)-120 fusion protein
- Granulocyte-macrophage colony-stimulating factor
- Gusperimus trihydrochloride
- Human IgG1Fc- iMod domain (amino acids 2-60) of human HARS fusion protein
- Human engineered monoclonal antibody specific for transforming growth factor ß1
- Human normal immunoglobulin
- Humanized IgG1 monoclonal antibody binding to CD19
- Inaxaplin
- Iodine (123I) Serum Amyloid P
- Iodine (124I) evuzamitide
- Iptacopan
- Ixazomib
- L-Pyr-L-Glu-L-Gln-L-Leu-L-Glu-L-Arg-L-Ala-L-Leu-L-Asn-L-Ser-L-Ser
- Lanifibranor
- Lenabasum
- Levamisol hydrochloride
- Mepolizumab
- N-(3,4-dihydroxyphenyl)-3,4-dihydroxybenzamide
- Nintedanib
- Nitric oxide
- Nitroglycerin
- PEGylated peptide inhibitor of complement C3
- Paquinimod
- Pegcetacoplan
- Peptide 144 TGF-beta1-inhibitor (TSLDASIIWAMMQN)
- Pioglitazone
- Pomalidomide
- Propagermanium
- Recombinant human minibody against complement component C5
- Recombinant human monoclonal antibody against mannan-binding lectin-associated serine protease-2
- Recombinant human residue 41 glutamic acid to glutamine variant of Interferon-alfa-2b
- Recombinant humanised anti-human interleukin-1 beta monoclonal antibody
- Recombinant humanized anti-transforming growth factor (TGF) beta 3 antibody
- Recombinant monoclonal antibody to human serum amyloid P component
- Rilonacept
- Riociguat
- Rituximab
- Romilkimab
- S3,S13-cyclo(D-tyrolsyl-L-isoleucyl-L-cysteinyl-L-valyl-1-methyl-L-tryptophyl-L-glutaminyl-L-aspartyl-L-tryptophyl-N-methyl-L-glycyl-L-alanyl-L-histidyl-L-arginyl-L-cysteinyl-N-methyl-L-isoleucinamide)
- Single stranded, chemically modified oligonucleotide that binds to and inhibits the function of micro RNA-21
- Siponimod
- Sodium thiosulfate
- Sparsentan
- Synthetic double-strand small interfering ribonucleic acid (siRNA) oligonucleotide drug directed against C3 messenger RNA
- Terguride
- Tocilizumab
- Treprostinil diethanolamine (oral use)
- Type I native bovine skin collagen
- Umbilical cord mesenchymal stem cell secretome
- autologous adipose tissue-derived stromal vascular fraction cells
- florbetaben (18F)
- humanised IgG1K monoclonal antibody against interferon beta
- imlifidase
- ziritaxestat
