Orphanet: Search for an orphan drug
Search for an orphan drug
47 Result(s)
3-(5-amino-2-methyl-4-oxoquinazolin-3(4H)-yl)piperidine-2,6-dione hydrochloride
5-(4,6-dimorpholino-1,3,5-triazin-2-yl)-4-(trifluoromethyl)pyridin-2-amine
Allogeneic multi-virus specific T lymphocytes targeting BK virus, cytomegalovirus, human herpesvirus-6, Epstein Barr virus and adenovirus
Autologous CD4+ and CD8+ T cells expressing a CD19-specific chimeric antigen receptor
Autologous engineered anti -CD19 Chimeric Antigen Receptor (CAR +) T -cells
Axicabtagene ciloleucel
Brentuximab vedotin
Enzastaurin hydrochloride
Everolimus
Humanised Fc engineered monoclonal antibody against CD19
Humanised anti-CD37 monoclonal antibody conjugated to maytansinoid DM1
Ibrutinib
Iodine (131I) tositumomab
Lenalidomide
Mocetinostat
Obinutuzumab
Pixantrone dimaleate
Polatuzumab vedotin
Pralatrexate
Recombinant histidine-tagged idiotype immunoglobulin Fab fragment of clonal B-cell receptors
Rituximab
Selinexor
Tazemetostat
Valproic acid, sodium
Venetoclax
haematopoietic stem cells and blood progenitors umbilical cord-derived expanded with (1R, 4R)-N1-(2-benzyl-7-(2-methyl-2H-tetrazol-5-yl)-9H-pyrimido[4,5-b]indol-4-yl)cyclohexane-1,4-diamine dihydrobromide dihydrate