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Substance(s)
- 1-(3-{4-[3,4-difluoro-2-(trifluoromethyl)phenyl]piperidine-1-carbonyl}-1H,4H,5H,6H,7H-pyrazolo[3,4-c]pyridin-6-yl)ethan-1-one
- 3-(3-(3,5-bis(trifluoromethyl)phenyl)-1h-pyrazol-1-yl)propanoic acid
- Adeno-associated viral vector serotype 5 containing the human ABCA4 gene
- Adeno-associated virus serotype 5 containing the human RDH12 gene
- Adeno-associated virus serotype 8 containing the human RdCVF sequence and the human RdCVFL sequence
- Combination of three adeno-associated viral vectors of serotype 8 containing the 5'-, the body- and the 3'- coding sequences of human CEP290 fused to inteins
- Combination of two adeno-associated viral vectors of serotype 8 containing the 5'- and the 3'- half coding sequences of human ABCA4 fused to inteins
- Echothiophate iodide
- Ecothiopate iodide
- Emixustat hydrochloride
- Human embryonic stem-cell-derived retinal pigment epithelial cells
- Lentiviral vector containing the human ABCA4 gene
- Ma09-Hrpe Cells
- Mixture of two adeno-associated viral vectors of serotye 8 containing the 5'-half sequence of human ABCA4 gene and the 3'-half sequence of human ABCA4 gene
- Ramiprilat
- Soraprazan