Search for an orphan drug
Other search option(s)
7 Result(s)
Substance(s)
- Allogeneic cultured postnatal thymus-derived tissue
- Autologous CD34+ cells transfected with a lentiviral vector containing codon optimised RPS19 gene
- Autologous CD34+ enriched cells transduced with a self-inactivating lentiviral vector containing the codon-optimized RPS19 gene
- Cannabidiol
- Miransertib
- Potassium iodide oral solution