Orphanet: Search for an orphan drug
Search for an orphan drug
60 Result(s)
2-{[2-benzyl-4-(5-methyl-3H-imidazol-4-ylmethyl)-3-oxo-piperazine-1-carbonyl]- amino}-4methyl-pentanoic acid
A-dmDT390-bisFv(UCHT1)
Adenovirus-Interferon gamma - coding DNA sequence
Alisertib
Allogeneic multi-virus specific T lymphocytes targeting BK virus, cytomegalovirus, human herpesvirus-6, Epstein Barr virus and adenovirus
Belinostat
Besilesomab
Brentuximab vedotin
Chlormethine
Darinaparsin
Denileukin diftitox
Duvelisib
Fenretinide
Forodesine hydrochloride
Human monoclonal antibody against CD4
Humanised IgG1 monoclonal antibody against human KIR3DL2
Iodine (131I) tositumomab
Ligand binding moiety to STAT3, a chemical linker, and a ligand binding moiety to an E3 ligase that leads to STAT3 degradation
Meclorethamine
Miltefosine
Mogamulizumab
N-(2-aminophenyl)-4-(1-[(1,3-dimethyl-1H-pyrazol-4-yl)methyl]piperidin)benzamide
Naloxone hydrochloride dihydrate
Nanatinostat, valganciclovir
Panobinostat
Pralatrexate
Recombinant anti-CD3-bi-single-chain-Fv-diphtheria toxin fusion protein
Resiquimod
Rituximab
Romidepsin
S-[5-(omega-methoxypoly(oxyethylene)-2-oxopentyl)]-L-cysteinylglycyl-L-serinylglycylgylcyl-L-isoleucyl-L-lysyl-L-glutamyl-L-phenylalanyl-L-leucyl-L-glutaminyl-L-arginyl-L-phenylalanyl-L-isoleucyl-L-histyl-L-isoleucyl-L-valyl-L-glutaminyl-L-serinyl-L-isoleucyl-L-isoleucyl-L-asparaginyl-L-threonyl-L-serinamide, acetate salt
Siplizumab
Suberolylanilide hydroxamic acid
Synthetic hypericin
Tipifarnib
Vorinostat
Zanolimumab
haematopoietic stem cells and blood progenitors umbilical cord-derived expanded with (1R, 4R)-N1-(2-benzyl-7-(2-methyl-2H-tetrazol-5-yl)-9H-pyrimido[4,5-b]indol-4-yl)cyclohexane-1,4-diamine dihydrobromide dihydrate
oligonucleotide inhibitor of microRNA miR-155-5p