Search for an orphan drug
72 Result(s)
- (5S,8S,10aR)-N-benzhydryl-5-((S)-2-(methylamino)propanamido)-3-(3-methylbutanoyl)-6-oxodecahydropyrrolo[1,2-a][1,5]diazocine-8-carboxamide
- 1-(4-{4-amino-7-[1-(2-hydroxyethyl)-1H-pyrazol-4-yl]thieno[3,2-c]pyridin-3-yl}phenyl)-3-(3-fluorophenyl)urea
- 2-Allyl-1-[6-(1-hydroxy-1-methylethyl)pyridin-2-yl]-6-{[4-(4-methylpiperazin-1-yl)phenyl]amino}-1,2-dihydro-3H-pyrazolo[3,4-d]pyrimidin-3-one
- 2-hydroxymethyl-2-methoxymethyl-1-azabicyclo[2,2,2]octan-3-one
- 20-pentaerythritol poly (oxy-1,2-ethanediyl)-carboxymethyl-glycinate-7-ethyl-10-hydroxycamptothecine 10-[1,4'-bipiperidine]-1'-carboxylate
- 8-[4-(1-aminocyclobutyl)phenyl]-9-phenyl-1,2,4-triazolo[3,4-f][1,6]naphthyridin-3(2H)-one mono-hydrochloride
- Abagovomab
- Ad5/3-D24-granulocyte-macrophage colony stimulating factor (GMCSF)-encoding oncolytic adenovirus
- Adenovirus-associated vector containing human Fas-c gene
- Albumin-binding prodrug of doxorubicin
- Alisertib
- Anti-EphA2 monoclonal antibody conjugated to maleimidocaproyl monomethylauristatin phenylalanine
- Anti-epithelial cell adhesion molecule / anti-CD3 monoclonal antibody
- Autologous dendritic cells pulsed with recombinant human-fusion protein (mucin 1 - glutathione S transferase) coupled to oxidised polymannose
- Bevacizumab
- Binimetinib
- Catumaxomab
- Cediranib
- Chimeric monoclonal antibody against claudin 6
- Cisplatin (liposomal)
- Defactinib
- Doxorubicin hydrochloride (pegylated liposomal)
- Folic acid to be used with N-[4-[[(2-amino-3,4-dihydro-4-oxo-6-pteridinyl)methyl]amino]benzoyl]-D-gamma-glutamyl-(2S)-2-amino-beta-alanyl-L-alpha-aspartyl-L-cysteine
- Fosbretabulin tromethamine
- Genetically modified serotype 5/3 adenovirus coding for granulocyte-macrophage colony-stimulating factor
- Human MHC non-restricted cytotoxic T-cell line
- Human milk fat globule 1 / Yttrium (90Y) human milk fat globule 1 - S-p-isothiocyanatobenzyl-diethylenetriaminepentaacetic acid
- Humanised monoclonal antibody to the folate receptor alpha
- Imexon
- Ketoconazole
- Lurbinectedin
- Maytansinoid-conjugated human monoclonal antibody against mesothelin
- Megestrol acetate
- Mibefradil
- Murine anti-idiotypic antibody against OC125 antibody against CA125 antigen
- N-(4-{3-(2-aminopyrimidin-4-yl)pyridin-2-yl]oxy}phenyl)-4-(4-methylthiophen-2-yl)phthalazin-1-amine bis-mesylate dihydrate
- N-[4-[[(2-amino-3,4-dihydro-4-oxo-6-pteridinyl)methyl]amino]benzoyl]-D-gamma-glutamyl-(2S)-2-amino-beta-alanyl-L-alpha-aspartyl-L-cysteine and folic acid
- Niraparib
- Olaparib
- Oregovomab
- Paclitaxel (micellar)
- Patupilone (Epothilone B)
- Plevitrexed
- Poly-CD-PEG-camptothecin
- Pyr-His-Trp-Ser-Tyr-D-Lys(doxorubicinylglutarate)-Leu-Arg-Pro-Gly-NH2, acetate salt
- Rucaparib
- Small molecule normalizing the p53 function
- Trabectedin
- Trebananib
- Treosulfan
- Vaccine consisting of 5 survivin peptides with different human leukocyte antigen restrictions
- Veliparib
- Vincaleukoblastin-23-oic acid, O4-deacetyl-2-[(2-mercaptoethoxy)carbonyl]hydrazide, disulfide with N-[4-[[(2-amino-3,4-dihydro-4-oxo-6-pteridinyl)methyl]amino]benzoyl]-L-gamma-glutamyl-L-alpha-aspartyl-L-arginyl-L-alpha-aspartyl-L-alpha-aspartyl-L-cysteine
- autologous dendritic cells pulsed with killed ovarian cancer cells and matured by TLR3 ligand ex vivo
- enadenotucirev
- human reovirus type 3 Dearing strain
- humanised anti-folate receptor 1 monoclonal antibody conjugated to maytansinoid DM4
- motolimod